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Gene Therapy Biotech Companies and Upcoming Catalysts

Public company snapshots and catalyst previews organized by modality.

Public Company List

TickerCompanyLead AssetIndicationStageNext Catalyst
TSHATaysha Gene TherapiesTSHA-102Rett SyndromePhase 32027-03-12
TELOTelomir Pharmaceuticals IncTargeting Metal-Dependent Epigenetic Dysregulationn/an/a2027-05
PASGPassage Bio IncPBFT02n/aPhase 1/22030-11-01
LGVNLongeveron IncAllogeneic MSCMild Alzheimer's DiseasePhase 2Corporate Update
MTNBMatinas Biopharma Holdings IncMAT2203general corporate purposesPhase 3Data Readout

Upcoming Catalysts

Company Ticker Catalyst Timing Asset Confidence
Mustang Bio Inc MBIO Clinical Trial Completion 2026-08-06 cyclophosphamide Low
Boundless Bio Inc BOLD Clinical Trial Completion 2026-09-30 BBI-355 Low
Taysha Gene Therapies TSHA Clinical Trial Completion 2027-03-12 TSHA-101 Low
Curis Inc CRIS Corporate Update October 2015 CA-170 Low

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